Adeno-associated viral gene therapy for mucopolysaccharidoses exhibiting neurodegeneration

Medicine and Dentistry

• Cell Enzyme 16%
• Central Nervous System 16%
• Clinical Trial 33%
• Diseases 16%
• Enzyme Replacement Therapy 16%
• Gene Therapy 16%
• Glycosaminoglycan 16%
• Hematopoietic Stem Cell Transplantation 16%
• Hunter Syndrome 16%
• Lysosomal Storage Disease 16%
• Mucopolysaccharidosis 100%
• Neurodegeneration 100%
• Sanfilippo Syndrome 16%
• Scheie Syndrome 16%
• Storage Disease 16%
• Viral Gene Therapy 100%
• Virus Vector 16%

Pharmacology, Toxicology and Pharmaceutical Science

• Clinical Trial 33%
• Diseases 16%
• Glycosaminoglycan 16%
• Hunter Syndrome 16%
• Lysosome Storage Disease 16%
• Mucopolysaccharidosis 100%
• Nerve Degeneration 100%
• Replacement Therapy 16%
• Sanfilippo Syndrome 16%
• Scheie Syndrome 16%
• Storage Disease 16%
• Viral Vector 16%

Biochemistry, Genetics and Molecular Biology

• Clinical Trial 33%
• Enzyme 16%
• Gene Therapy 100%
• Glycosaminoglycan 16%
• Hematopoietic Stem Cell Transplantation 16%
• Hunter Syndrome 16%
• Mucopolysaccharidosis 100%
• Sanfilippo Syndrome 16%
• Virus Vector 16%