Lentiviral-mediated gene therapy for murine mucopolysaccharidosis type IIIA

Chantelle McIntyre, Ainslie Derrick Roberts, Enzo Ranieri, Peter Clements, Sharon Byers, Donald Anson

    Research output: Contribution to journalArticlepeer-review

    28 Citations (Scopus)
    Original languageEnglish
    Pages (from-to)411-418
    Number of pages8
    JournalMolecular Genetics and Metabolism
    Volume93
    Issue number4
    Publication statusPublished - 2008

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