Low-dose, continuous enzyme replacement therapy ameliorates brain pathology in the neurodegenerative lysosomal disorder mucopolysaccharidosis type IIIA

Barbara King, Sofia Hassiotis, Tina Rozaklis, Helen Beard, Paul J. Trim, Marten F. Snel, John J. Hopwood, Kim M. Hemsley

Research output: Contribution to journalArticlepeer-review

11 Citations (Scopus)

Fingerprint

Dive into the research topics of 'Low-dose, continuous enzyme replacement therapy ameliorates brain pathology in the neurodegenerative lysosomal disorder mucopolysaccharidosis type IIIA'. Together they form a unique fingerprint.

Medicine & Life Sciences

Chemical Compounds