Slow, continuous enzyme replacement via spinal CSF in dogs with the paediatric-onset neurodegenerative disease, MPS IIIA

Barbara King, Neil R. Marshall, Sofia Hassiotis, Paul J. Trim, Justin Tucker, Kathryn Hattersley, Marten F. Snel, Robert D. Jolly, John J. Hopwood, Kim M. Hemsley

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16 Citations (Scopus)

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Neuroscience

Pharmacology, Toxicology and Pharmaceutical Science